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Treatment
Betibeglogene Autotemcel (Beti-cel / Zynteglo)
1
Conditions
5
Trials
300
Participants
35%
Average Safety
Condition Evidence
Thalassemias
5 trials Β· 300 participants
90% effectiveness Β· 35% safety
Betibeglogene Autotemcel (Beti-cel / Zynteglo) | DFDA