Condition

G6PD deficiency

Clinical trials and treatment information for G6PD deficiency

443.3M
People Affected
60
Active Trials
3M
New Cases/Year
8,087
Deaths/Year

Treatment Rankings

Ranked by evidence volume first. Medicine has spent centuries ranking things by vibes. This is an improvement.

1
Avoidance of Oxidative Stressors (e.g., Fava Beans, Sulfa Drugs, Antimalarials)
95% Effectivenessβ€’ 90% Confidenceβ€’ 100% Safety00
HIGH EvidenceExcellent ValueDose: Strict adherence to known trigger avoidance lists
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Comparative Safety Scale(Higher is safer)

Cyanide☠️
MethπŸ’€
Cigarettes🚬
Chemo☒️
Alcohol🍺
MorphineπŸ’Š
AntibioticsπŸ’‰
TylenolπŸ’Š
ExerciseπŸƒ
WaterπŸ’§
100
DangerousModerateSafe

Time to Effect

Immediate (upon avoidance)

Duration

Lifetime

Response Rate

100%

Remission Rate

100%

Annual Cost of Care

Drug Cost

$0

Monitoring

$1,500

Side Effects

$0

Total Annual

$1,500

Cost-Effectiveness

EXCELLENT

QALYs Gained

0.8

000
Treatment Outcomes
Efficacy Outcomes
Overall Effectiveness
+95%
Response Rate
+100%
Remission Rate
+100%
2
Blood Transfusion (for acute severe hemolysis)
90% Effectivenessβ€’ 95% Confidenceβ€’ 65% Safety00
HIGH EvidenceExcellent ValueDose: Varies by patient's hemoglobin level and clinical status
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Comparative Safety Scale(Higher is safer)

Cyanide☠️
MethπŸ’€
Cigarettes🚬
Chemo☒️
Alcohol🍺
MorphineπŸ’Š
AntibioticsπŸ’‰
TylenolπŸ’Š
ExerciseπŸƒ
WaterπŸ’§
65
DangerousModerateSafe

Time to Effect

Immediate (within hours of administration)

Duration

As needed during acute hemolytic crisis (typically 1-2 units over several hours)

Response Rate

95%

Remission Rate

%

Common Side Effects:

Febrile non-hemolytic transfusion reaction: 1%
Allergic reaction: 0.5%
Delayed hemolytic transfusion reaction: 0.05%
Transfusion-associated circulatory overload (TACO): 0.05%
Transfusion-related acute lung injury (TRALI): 0.01%
Infection (e.g., HIV, HCV, HBV): 0.0001%

Annual Cost of Care

Drug Cost

$0

Monitoring

$1,500

Side Effects

$0

Total Annual

$1,500

Cost-Effectiveness

EXCELLENT

QALYs Gained

5

Treatment Outcomes
Efficacy Outcomes
Overall Effectiveness
+90%
Response Rate
+95%
Common Side Effects
Febrile non-hemolytic transfusion reaction
+1%
Allergic reaction
+0.5%
Delayed hemolytic transfusion reaction
+0.05%
3
Folic Acid Supplementation
85% Effectivenessβ€’ 90% Confidenceβ€’ 90% Safetyβ€’ 50 trialsβ€’ 10K participants
MODERATE EvidenceExcellent ValueDose: 1 mg daily
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Comparative Safety Scale(Higher is safer)

Cyanide☠️
MethπŸ’€
Cigarettes🚬
Chemo☒️
Alcohol🍺
MorphineπŸ’Š
AntibioticsπŸ’‰
TylenolπŸ’Š
ExerciseπŸƒ
WaterπŸ’§
90
DangerousModerateSafe

Time to Effect

Weeks to months (to normalize folate levels and support erythropoiesis)

Duration

Lifetime (for patients with chronic hemolysis)

Response Rate

100%

Remission Rate

%

Common Side Effects:

Nausea: 0.1%
Bloating: 0.1%

Annual Cost of Care

Drug Cost

$10

Monitoring

$1,500

Side Effects

$0

Total Annual

$1,510

Cost-Effectiveness

EXCELLENT

QALYs Gained

0.05

ICER

$100/QALY

Treatment Outcomes
Efficacy Outcomes
Overall Effectiveness
+85%
Response Rate
+100%
Common Side Effects
Nausea
+0.1%
Bloating
+0.1%